The company also noted that the label update meets an unmet need, with up to 80% of patients with atherosclerotic cardiovascular disease (ASCVD) facing challenges in achieving the LDL-C guideline-recommended target of less than 70 mg/dL.1
Background and Previous FDA Approvals
Leqvio was first approved by the FDA on December 22, 2021, as the first and only small interfering RNA to reduce LDL-C with two doses a year, after an initial dose and one at three months.2
This latest FDA label update for Leqvio isn’t its first expansion, as it's part of an ongoing effort to expand the therapy’s use and reinforce its role in LDL-C management. On July 10, 2023, the FDA approved a label update for the drug to enable earlier use in patients with elevated LDL-C who have an increased risk of heart disease, as an adjunct to diet and statin therapy. Additional label changes included eliminating the Limitations of Use statement and streamlining the safety section by removing four adverse events (AEs), as their occurrence rates matched those seen in the placebo group.3
Safety Profile and Contraindications
Common AEs reported in clinical trials for Leqvio included injection site reaction, arthralgia, and bronchitis. Novartis warns that Leqvio is contraindicated in patients with a prior serious hypersensitivity reaction to inclisiran or any of the excipients in Leqvio. Additionally, Leqvio should be discontinued during pregnancy due to potential fetal harm based on its mechanism of action, and because lipid-lowering treatment is generally not necessary during this time.4
Cardiovascular Disease Burden and Corporate Strategy
According to Novartis, ASCVD accounts for approximately 85% of all cardiovascular deaths, with a burden higher than any other chronic disease in the United States. Cardiovascular disease (CVD) leads to more deaths than cancer, chronic lung disease, and diabetes combined. However, an estimated 80% of premature cardiovascular deaths could be avoided by targeting the underlying causes and risk factors of CVD.1
Novartis initially acquired the rights to develop, manufacture, and commercialize Leqvio through a licensing and collaboration agreement with Alnylam Pharmaceuticals.2
"Novartis is committed to addressing the rising burden of cardiovascular disease, a substantial public health burden affecting 30 million Americans," said Bulto, in a July 2023 press release. "High LDL-C is one of the most readily modifiable risk factors for heart disease and this label update for Leqvio will help us reach a greater number of patients who struggle with lowering their LDL-C."3
References
- Novartis twice-yearly* Leqvio® (inclisiran) receives FDA approval for new indication enabling first-line use. PR Newswire. July 31, 2025. Accessed August 1, 2025. https://www.prnewswire.com/news-releases/novartis-twice-yearly-leqvio-inclisiran-receives-fda-approval-for-new-indication-enabling-first-line-use-302519118.html
- FDA Approves Leqvio. Drugs.com. Accessed August 1, 2025. https://www.drugs.com/newdrugs/fda-approves-leqvio-inclisiran-first-class-sirna-reduce-low-density-lipoprotein-cholesterol-ldl-c-5760.html
- US FDA Approves Expanded Indication for Leqvio (inclisiran) to Include Treatment of Adults with High LDL-C and Who Are At Increased Risk of Heart Disease. Drugs.com. Accessed August 1, 2025. https://www.drugs.com/newdrugs/us-fda-approves-expanded-indication-leqvio-inclisiran-include-adults-ldl-c-increased-risk-heart-6057.html
- HIGHLIGHTS OF PRESCRIBING INFORMATION. Novartis. Accessed August 1, 2025. https://www.novartis.com/sites/novartis_us/files/leqvio.pdf